Abstract

Gene therapy can be defined as the introduction of genetic material into a particular cell or tissue type to alter the pattern of gene expression to produce a therapeutic effect. There are three critical components to consider in designing and optimizing a gene therapy strategy for the treatment of any disease: a vector to introduce the gene, a device and procedure for delivering the vector to the appropriate tissue or organ, and a therapeutic gene. Each component must be chosen or modified to best suit the specific characteristics of the particular disease of interest.

Full Text
Paper version not known

Talk to us

Join us for a 30 min session where you can share your feedback and ask us any queries you have

Schedule a call