Abstract

Article history: Received 3 December 2015 Accepted 3 December 2015 Available online 3 December 2015 trophin protein. Two groups recently published data, a single-dose intravascular delivery of rAAV2/8-Spc512-μDys (Le Guiner et al., 2015) and AAV-9 reporter or micro-dystrophin (μDys) vector at doses of 1.92–6.24 × 10 viral genome particles/kg (Yue et al., 2015) in Golden Retriever Muscular Dystrophy Dogs, the canine model of DMD. Overall, the improvement of multiple muscle parameters was observed with no

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