Abstract
The past five years have yielded many important advances in care, treatment and lifespan for individuals living with spinal muscular atrophy (SMA). Despite these improvements in research and innovation, it is important to understand outcomes that matter most to patients and ways to measure changes that can be used in clinical care and research settings. Health-related quality of life (HRQOL) measurement instruments enable benchmarking and assessing changes across populations.
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Schedule a callMore From: Value in health : the journal of the International Society for Pharmacoeconomics and Outcomes Research
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