Abstract
Spinal muscular atrophy (SMA) is a rare, progressive neuromuscular disorder that causes muscle weakness and systemic disease-related complications. Utilities (measures of health-related quality of life [HRQoL]), costs and healthcare resource use (HCRU) are often reported according to SMA type; however, recent literature suggests an association between HCRU and patient motor ability. The objective of this study was to describe HRQoL and HCRU according to motor function health states of patients with SMA.
Full Text 
Sign-in/Register to access full text options
Sign-in/Register to access full text options 
Published version (
Free)
Free) 
Talk to us
Join us for a 30 min session where you can share your feedback and ask us any queries you have
Schedule a callMore From: Value in health : the journal of the International Society for Pharmacoeconomics and Outcomes Research
Paper Title
Journal
Date
