Retrovirus-mediated transfer of the cDNA for human glucocerebrosidase into peripheral blood repopulating cells of patients with Gaucher's disease.

Abstract

Human Gene TherapyVol. 8, No. 17 News and CommentsRetrovirus-Mediated Transfer of the cDNA for Human Glucocerebrosidase into Peripheral Blood Repopulating Cells of Patients with Gaucher's Disease. University of Wisconsin, Madison, WisconsinPrincipal Investigator Friedrich SchueningPrincipal Investigator Friedrich SchueningSearch for more papers by this authorPublished Online:20 Mar 2008https://doi.org/10.1089/hum.1997.8.17-2143AboutSectionsPDF/EPUB ToolsPermissionsDownload CitationsTrack CitationsAdd to favorites Back To Publication ShareShare onFacebookTwitterLinked InRedditEmail FiguresReferencesRelatedDetailsCited byApplications of Gene TherapyGene therapy for β-thalassaemia: the continuing challenge1 October 2010 | Expert Reviews in Molecular Medicine, Vol. 12Therapy for Gaucher disease: Don’t stop thinking about tomorrowMolecular Genetics and Metabolism, Vol. 90, No. 2The evolving role of gene-based treatment in surgery4 November 2005 | British Journal of Surgery, Vol. 92, No. 12A review of gene therapy for haematological disordersBritish Journal of Haematology, Vol. 128, No. 1The Current Status of Gene Therapy in Autologous Transplantation2 November 2005 | Acta Haematologica, Vol. 114, No. 4Cell-based therapies for birth defects: A role for adult stem cell plasticity?25 August 2003 | Birth Defects Research Part C: Embryo Today: Reviews, Vol. 69, No. 3Macrophage-Specific Gene Targeting In VivoHematopoietic stem cell gene therapy for inherited bone marrow disorders: Past accomplishments and continued challenges16 May 2002 | Journal of Cellular Biochemistry, Vol. 85, No. S38Gene therapy for genetic haematological disorders and immunodeficienciesJournal of Internal Medicine, Vol. 249, No. 4Current Status of Retroviral Vector Mediated Gene Transfer into Human Hematopoietic Stem Cells1 July 2009 | Leukemia & Lymphoma, Vol. 41, No. 1-2Current Status of Retroviral Vector Mediated Gene Transfer into Human Hematopoietic Stem Cells1 July 2009 | Leukemia & Lymphoma, Vol. 41, No. 5-6Mild preconditioning and low-level engraftment confer methotrexate resistance in mice transplanted with marrow expressing drug-resistant dihydrofolate reductase activityBlood, Vol. 96, No. 4Mild preconditioning and low-level engraftment confer methotrexate resistance in mice transplanted with marrow expressing drug-resistant dihydrofolate reductase activityBlood, Vol. 96, No. 4Viral Vectors for Gene TransferDrugs, Vol. 60, No. 2Towards metabolic sink therapy for mut methylmalonic acidaemia: Correction of methylmalonyl-CoA mutase deficiency in T lymphocytes from a mut methylmalonic acidaemia child by retroviral-mediated gene transfer1 October 1999 | Journal of Inherited Metabolic Disease, Vol. 22, No. 7Transfert génique à visée thérapeutique dans les cellules souches hématopoïétiques et les cellules du système immunitaireAnnales de l'Institut Pasteur / Actualités, Vol. 10, No. 3-4Gene therapy for lysosomal storage diseases23 February 2005 | Expert Opinion on Investigational Drugs, Vol. 7, No. 10 Volume 8Issue 17Nov 1997 InformationCopyright 1997, Mary Ann Liebert, Inc.To cite this article:Principal Investigator Friedrich Schuening.Retrovirus-Mediated Transfer of the cDNA for Human Glucocerebrosidase into Peripheral Blood Repopulating Cells of Patients with Gaucher's Disease. University of Wisconsin, Madison, Wisconsin.Human Gene Therapy.Nov 1997.2143-2160.http://doi.org/10.1089/hum.1997.8.17-2143Published in Volume: 8 Issue 17: March 20, 2008PDF download