Recombinant adenovirus gene transfer in adults with partial ornithine transcarbamylase deficiency (OTCD).

Abstract

Human Gene TherapyVol. 10, No. 14 Recombinant Adenovirus Gene Transfer in Adults with Partial Ornithine Transcarbamylase Deficiency (OTCD)Mark L. Batshaw, James M. Wilson, Steven Raper, Marc Yudkoff, and Michael B. RobinsonMark L. BatshawSearch for more papers by this author, James M. WilsonSearch for more papers by this author, Steven RaperSearch for more papers by this author, Marc YudkoffSearch for more papers by this author, and Michael B. RobinsonSearch for more papers by this authorPublished Online:6 Jul 2004https://doi.org/10.1089/10430349950017068AboutSectionsPDF/EPUB ToolsPermissionsDownload CitationsTrack CitationsAdd to favorites Back To Publication ShareShare onFacebookTwitterLinked InRedditEmail FiguresReferencesRelatedDetailsCited byAbnormalities of Hepatic Protein MetabolismAdenoviral Vector-Based Vaccines and Gene Therapies: Current Status and Future Prospects13 March 2019Spliced: Boundary-work and the establishment of human gene therapy28 June 2017 | BioSocieties, Vol. 12, No. 2Adenoviruses7 March 2016The Ethics of Randomized Trials in Oncology25 November 2014Turning the Corner with Viral-based Gene Therapy—Development of the Rogue BiopharmaceuticalGene TherapyVirus-mediated gene delivery for human gene therapyJournal of Controlled Release, Vol. 161, No. 2Radioprotective gene therapy2 May 2011 | Expert Opinion on Biological Therapy, Vol. 11, No. 9The Death of Jesse Gelsinger: New Evidence of the Influence of Money and Prestige in Human Research1 June 2010 | American Journal of Law & Medicine, Vol. 36, No. 2-3Complement Component C1q and Anti-hexon Antibody Mediate Adenovirus Infection of a CAR-Negative Cell Line Van Tsai, Robin Varghese, Sundari Ravindran, Robert Ralston, and Gary Vellekamp30 December 2008 | Viral Immunology, Vol. 21, No. 4The gene delivery system for rheumatoid synoviumJapanese Journal of Clinical Immunology, Vol. 31, No. 1Gene therapy. 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Robinson.Recombinant Adenovirus Gene Transfer in Adults with Partial Ornithine Transcarbamylase Deficiency (OTCD).Human Gene Therapy.Sep 1999.2419-2437.http://doi.org/10.1089/10430349950017068Published in Volume: 10 Issue 14: July 6, 2004PDF download