OP0231 EFFICACY AND SAFETY OF AZACITIDINE FOR PATIENTS WITH VEXAS SYNDROME: RETROSPECTIVE STUDY FROM THE FRENVEX

Abstract

Background:VEXAS (Vacuoles, E1 Enzyme, X-linked, Autoinflammatory, Somatic) syndrome is a severe autoinflammatory disease in adults resulting from somatic mutations in the UBA1 gene, associated with myelodysplastic syndromes (MDS) in 40-50%...