Favorable Outcomes in Pediatric Patients in the Phase 3 Hgb-207 (Northstar-2) and Hgb-212 (Northstar-3) Studies of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia

Alexis A Thompson,Janet L Kwiatkowski,John B Porter,Suradej Hongeng,Evangelia Yannaki,Andreas E Kulozik,Martin G Sauer,Adrian J Thrasher,Isabelle Thuret,Ashutosh Lal,Ruiting Guo,Weijian Liu,Richard A Colvin,Mark C Walters,Franco Locatelli

doi:10.1182/blood-2020-135857

Favorable Outcomes in Pediatric Patients in the Phase 3 Hgb-207 (Northstar-2) and Hgb-212 (Northstar-3) Studies of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia

Alexis A Thompson, Janet L Kwiatkowski + Show 13 more

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https://doi.org/10.1182/blood-2020-135857

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Journal: Blood	Publication Date: Nov 5, 2020
Citations: 10

Affiliation: Lurie Children's Hospital, University of Pennsylvania, Children's Hospital of Philadelphia, University College London, Ramathibodi Hospital, G. Papanikolaou General Hospital, Heidelberg University, European Molecular Biology Laboratory, Hochschule Hannover, Hannover Medical School, Great Ormond Street Hospital, Hôpital de la Timone, UCSF Benioff Children's Hospital, Bluebird Bio (United States), Bambino Gesù Children's Hospital

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Favorable Outcomes in Pediatric Patients in the Phase 3 Hgb-207 (Northstar-2) and Hgb-212 (Northstar-3) Studies of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia

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