Abstract

A solid start for gene therapy in Tay-Sachs disease.

Full Text
Paper version not known

Talk to us

Join us for a 30 min session where you can share your feedback and ask us any queries you have

Schedule a call

Similar Papers

Paper Title
Journal
Date
Author
Adeno-Associated Virus Gene Therapy in a Sheep Model of Tay-Sachs Disease.
...
Human gene therapy methods | VOL. 29
, et. al. ...
18 Sep 2017
A direct gene transfer strategy via brain internal capsule reverses the biochemical defect in Tay–Sachs disease
S Martino ... B Tancini
Human Molecular Genetics | VOL. 14
S Martino, et. al.S Martino ... B Tancini
22 Jun 2005
Late‐onset Tay–Sachs disease: The spectrum of peripheral neuropathy in 30 affected patients
Barbara E Shapiro ... Edwin H Kolodny
Muscle & nerve | VOL. 38
Barbara E Shapiro, et. al.Barbara E Shapiro ... Edwin H Kolodny
28 Jul 2008
Molecular Genetics of β-N-Acetylhexosaminidase α Subunit Mutations
Kousaku Ohno ... Kunihiko Suzuki
-
Kousaku Ohno, et. al.Kousaku Ohno ... Kunihiko Suzuki
01 Jan 1987
View more papers

More From: Nature Medicine

Paper Title
Journal
Date
Author
Proteomic aging clock predicts mortality and risk of common age-related diseases in diverse populations.
M Austin Argentieri ... Cornelia M Van Duijn
Nature Medicine | VOL. -
M Austin Argentieri, et. al.M Austin Argentieri ... Cornelia M Van Duijn
08 Aug 2024
Proteomic aging signatures predict disease risk and mortality across diverse populations.
-
Nature Medicine | VOL. -
--
08 Aug 2024
From neoadjuvant to organ-sparing immunotherapy for colorectal cancer.
Benoit Rousseau ... Luis A Diaz
Nature Medicine | VOL. -
Benoit Rousseau, et. al.Benoit Rousseau ... Luis A Diaz
08 Aug 2024
A generalist vision-language foundation model for diverse biomedical tasks.
Kai Zhang ... Lichao Sun
Nature Medicine | VOL. -
Kai Zhang, et. al.Kai Zhang ... Lichao Sun
07 Aug 2024
View more papers