Abstract
To the Editor: We read with interest the letter by Dr Reuser titled “Inconsistent Reporting About Dosing, Dosing Regimen, and Immunomodulation Therapy in Pompe Disease.”1 In our 2001 article, “Recombinant Human Acid α-Glucosidase Enzyme Therapy for Infantile Glycogen Storage Disease Type II: Results of a Phase I/II Clinical Trial,”2 we had reported the initial use of recombinant human acid α-glucosidase (rhGAA) in three infantile patients with Pompe disease.
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